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Phase 2 Study of A Novel Ammonia Scavenging Agent In Adults With Urea Cycle Disorders (UCDs)

Note: Authors are listed in contributing order.
Collection:ACMG2009
Authors and Institutions:Lee, Brendan (Baylor College of Medicine)
Mian, Asad (Baylor College of Medicine)
Shchelochkov, Oleg (Baylor College of Medicine)
Martinez, Toni (Hyperion Therapeutics, Inc.)
Mokhtarani, Masoud (Hyperion Therapeutics, Inc.)
Scharschmidt, Bruce (Hyperion Therapeutics, Inc.)
Diaz, George (Mount Sinai School of Medicine)
Rhead, William (Medical College of Wisconsin)
Berry, Susan (University of Minnesota)
Keywords:Metabolic Disorder
Topic:Clinical
Abstract Number:17
Session Date:08:00 AM-10:00 AM Friday, March 27, 2009
Files:Click Here to download PDF (ACMG2009-000002.pdf)

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